Rett Syndrome, the most physically disabling of the autism spectrum disorders, is caused by mutations in the methyl CpG-binding protein (MeCP2). Rett Syndrome…
Parkinson's Disease, brought to public awareness by figures such as Michael J. Fox, is not just difficult to diagnose. It's also difficult to accurately…
The mechanics of instinctive behavior are mysterious. Even something as simple as the question of how a mouse can use its powerful sense of smell to detect and…
Patients receiving a high dose of the therapy, called SERCA2a, experienced substantial clinical benefit and significantly reduced cardiovascular…
Using an innovative gene therapy technique called genome editing that hones in on the precise location of mutated DNA, scientists have treated the blood…
The Institute researchers, Douglas P. Kiel, M.D., M.P.H., and David Karasik, Ph.D., who are working with the Framingham Heart Study, identified a gene that is…